Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

Market OverviewThe global cell and gene therapy market is undergoing rapid and transformative growth, reflecting its increasing importance in modern healthcare.The market is projected to expand at a ...

A "gene silencer" (technically known as small interfering RNA, or siRNA), locally delivered by nanoparticles embedded in an ...

At a Food and Drug Administration cell and gene therapy (CGT) roundtable last June, most speakers pushed for the agency to ...

Experimental gene therapies like AMT‑130 lower toxic huntingtin protein and significantly slow Huntington’s disease, offering ...

Researchers have developed a gene therapy that significantly slowed motor function loss in preclinical models of amyotrophic lateral sclerosis (ALS), offering new hope for treating the devastating ...

University of California San Diego-led team has discovered that restoring a key cardiac protein called connexin‑43 in a mouse ...

Eli Lilly plans to expand its hearing loss therapy pipeline by collaborating with Seamless Therapeutics to apply the company’s next-generation gene-editing approach, based on programmable recombinases ...

The cochlea is the spiral-shaped structure within the inner ear responsible for our sense of hearing. To fully understand hearing functions and open the door to new hearing loss treatments, scientists ...

Avista Therapeutics expands AI gene therapy platform to break barriers in the delivery of genetic medicines: Pittsburgh Monday, January 12, 2026, 16:00 Hrs [IST] Avista Therapeuti ...

A protective APOE gene variant is enriched in Super Agers—people over 80 who think like 50‑year‑olds—cutting Alzheimer’s risk ...

Gene therapy for weight loss is being explored as a potential game-changer, with therapy aiming to program the body to ...